Oligodendrocyte Gene Therapy for Canavan Disease – Phase 1/2 Trial
- Okay, here's a breakdown of the references you provided, formatted for clarity.
- * Title: Adeno-associated virus-mediated gene therapy in a patient wiht Canavan disease using dual routes of administration adn immune modulation * Journal: Mol.
- * Title: The natural history of Canavan disease: 23 new cases and comparison with patients from literature * Journal: Orphanet J.
Okay, here’s a breakdown of the references you provided, formatted for clarity. I’ve extracted the key information from each entry.
Reference 29:
* Authors: Corti, M. et al.
* Title: Adeno-associated virus-mediated gene therapy in a patient wiht Canavan disease using dual routes of administration adn immune modulation
* Journal: Mol. Ther. Methods Clin.Dev.
* Year: 2023
* Volume: 30
* Pages: 303-314
* DOI: 10.1016/j.omtm.2023.06.001
* Links:
* Google Scholar
Reference 30:
* Authors: Bley, A. et al.
* Title: The natural history of Canavan disease: 23 new cases and comparison with patients from literature
* Journal: Orphanet J. Rare Dis.
* Year: 2021
* Volume: 16
* Pages: 227
* DOI: 10.1186/s13023-020-01659-3
* PubMed ID: 34011350
* PubMed Central Link: http://www.ncbi.nlm.nih.gov/pmc/articles/PMC8132415
* Links:
* article
* PubMed
* PubMed Central
I hope this is helpful! Let me know if you’d like me to do anything else with this information.