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Tag: Motor neuron disease

Intrathecal Onasemnogene abeparvovec for Spinal Muscular Atrophy Treatment-Experienced Patients

January 28, 2026

Intrathecal Onasemnogene abeparvovec for Spinal Muscular Atrophy Treatment-Experienced Patients

Onasemnogene abeparvovec for Treatment-Experienced SMA Patients: Phase 3b Trial Results

December 9, 2025

Onasemnogene abeparvovec for Treatment-Experienced SMA Patients: Phase 3b Trial Results

Intrathecal Onasemnogene abeparvovec for Spinal Muscular Atrophy

December 8, 2025

Intrathecal Onasemnogene abeparvovec for Spinal Muscular Atrophy

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