Gene Therapy Offers Hope for Infants with Rare Disorder
- * Title: Intravenous AAV9-ATP7Aplus subcutaneous copper histidinate optimizes outcomes in a lethal Menkes disease mouse model * Authors: Lalitha Venkataraman et al.
- * Provided by: Columbia University Irving Medical Centre * Website: https://www.cuimc.columbia.edu/
- * Title: Gene therapy may offer new hope for infants with rare, fatal disorder * Date of Publication: October 30, 2025 * Date of Retrieval: October...
Here’s a breakdown of the information provided in the text:
Research Article:
* Title: Intravenous AAV9-ATP7Aplus subcutaneous copper histidinate optimizes outcomes in a lethal Menkes disease mouse model
* Authors: Lalitha Venkataraman et al.
* Journal: Science Advances
* Publication Year: 2025
* DOI: 10.1126/sciadv.adw5612
* Link: https://dx.doi.org/10.1126/sciadv.adw5612
Source of Information:
* Provided by: Columbia University Irving Medical Centre
* Website: https://www.cuimc.columbia.edu/
News Article Citation (for print):
* Title: Gene therapy may offer new hope for infants with rare, fatal disorder
* Date of Publication: October 30, 2025
* Date of Retrieval: October 30, 2025
In essence, this text describes a research article published in Science Advances about a potential gene therapy for Menkes disease, and it indicates that the information is being shared via a news release from Columbia University irving medical Center.