Gene Therapy Trial: FDA Approves Research for Rare Diseases
- Here's a breakdown of the information provided, formatted for clarity:
- How to create personalized gene editing platforms: Next steps toward interventional genetics.
- * Title: Researchers to test gene therapy for rare diseases with a new FDA trial protocol * Date: November 14, 2025 (both published and retrieved date) * Source:...
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Publications Referenced:
* Ahrens-Nicklas et al. (2025). How to create personalized gene editing platforms: Next steps toward interventional genetics. The American Journal of human Genetics. DOI: 10.1016/j.ajhg.2025.10.006
* Prasad et al. (2025). FDA’s New Plausible Mechanism Pathway. New England Journal of Medicine. DOI: 10.1056/nejmsb2512695
Article Information:
* Title: Researchers to test gene therapy for rare diseases with a new FDA trial protocol
* Date: November 14, 2025 (both published and retrieved date)
* Source: The Philadelphia Inquirer, LLC. Distributed by Tribune Content Agency, LLC.
* Copyright: 2025 The Philadelphia Inquirer, LLC.
Citation (for print):
Researchers to test gene therapy for rare diseases with a new FDA trial protocol (2025, November 14) retrieved 14 November 2025