Tag: rare disease

May 14, 2026

Breakthrough Base Editing Cures Deadly Dravet Syndrome in Mice

December 8, 2025

Dyne Submits New Duchenne Drug to FDA Approval

October 4, 2025

Congenital Myopathy Gene Discovery – New Research Reveals Cause

September 23, 2025

Kidney Protein Stabilization Drug – Breakthrough Treatment

September 19, 2025

Barth Syndrome Treatment Approved by Regulators

September 17, 2025

Regeneron Drug Slows Bone Growth in Rare Disease

September 10, 2025

Golimumab & PsA: Reduced Corticosteroid Use

September 4, 2025

7 Pulmonology Headlines – August 2025

September 4, 2025

Bimekizumab: Psoriasis Treatment Outperforms Active Comparators

August 29, 2025

ACC Respiratory Disease Vaccination Guidelines for Adults with Heart Disease

August 27, 2025

World Allergy Organization Updates NSAID Hypersensitivity Classification

August 21, 2025

Esketamine Dexmedetomidine Sleep Insomnia Depression

August 21, 2025

Dyslipidemia Parkinson’s Risk: Metabolic Syndrome Connection

August 20, 2025

Food Allergy Treatment: Efficacy Over Method & Frequency

August 19, 2025

Systemic Inflammation & Healthcare Costs: ASCVD, CKD

August 6, 2025

Prime Editing Reverses Symptoms of Childhood Neurological Disease